Diagnosis and Emerging Treatment Strategies for Mucopolysaccharidosis VII (Sly Syndrome)

Fabiano de Oliveira Poswar,1- 4 Johanna Henriques Nehm,1 Francyne Kubaski,5 Edina Poletto,6 Roberto Giugliani1- 4,7- 9 1Clinical Research Group in Medical Genetics, Clinical Research Center, Hospital de Clínicas de Porto Alegre, Porto Alegre, RS, Brazil; 2Medical Genetics Service, Hospital de Clinic...

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Main Authors: Poswar FDO (Author), Henriques Nehm J (Author), Kubaski F (Author), Poletto E (Author), Giugliani R (Author)
Format: Book
Published: Dove Medical Press, 2022-12-01T00:00:00Z.
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