Hematopoietic Stem Cell Transplant for the Treatment of X-MAID

• Main Authors: Sarah E. Henrickson (Author), Isabelle Andre-Schmutz (Author), Chantal Lagresle-Peyrou (Author), Matthew A. Deardorff (Author), Harumi Jyonouchi (Author), Benedicte Neven (Author), Nancy Bunin (Author), Jennifer R. Heimall (Author)
• Format: Book
• Published: Frontiers Media S.A., 2019-05-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

We report outcomes after hematopoietic stem cell transplant for three patients with X-MAID, including 1 patient from the originally described cohort and two brothers with positive TREC newborn screening for SCID who were found to have a T-B-NK+ SCID phenotype attributable to X-linked moesin associat...