Implementation and results of a risk-sharing scheme for enzyme replacement therapy in lysosomal storage diseases

• Päätekijät: María Dolores Edo-Solsona (Tekijä), José Luis Poveda-Andrés (Tekijä), Isidro Vitoria-Miñana (Tekijä)
• Aineistotyyppi: Kirja
• Julkaistu: Elsevier, 2020-01-01T00:00:00Z.
• Aiheet: article
• Linkit: Connect to this object online.

Objective: To describe a risk-sharing program's implementation and results on enzyme replacement therapy for lysosomal diseases. Method: The program was designed and implemented in a referral hospital for congenital metabolic diseases. The conclusion of agreements required the following phases:...