Treatment of Cystic Fibrosis: From Gene- to Cell-Based Therapies

Prognosis of patients with cystic fibrosis (CF) varies extensively despite recent advances in targeted therapies that improve CF transmembrane conductance regulator (CFTR) function. Despite being a multi-organ disease, extensive lung tissue destruction remains the major cause of morbidity and mortal...

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Autors principals: Katelin M. Allan (Autor), Nigel Farrow (Autor), Martin Donnelley (Autor), Adam Jaffe (Autor), Shafagh A. Waters (Autor)
Format: Llibre
Publicat: Frontiers Media S.A., 2021-03-01T00:00:00Z.
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3rd Floor Main Library

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