Real-world experience of emicizumab prophylaxis in young children with hemophilia A: retrospective data from China

• Prif Awduron: Guoqing Liu (Awdur), Kun Huang (Awdur), Gang Li (Awdur), Yingzi Zhen (Awdur), Zhengping Li (Awdur), Zhenping Chen (Awdur), Runhui Wu (Awdur)
• Fformat: Llyfr
• Cyhoeddwyd: Frontiers Media S.A., 2022-10-01T00:00:00Z.
• Pynciau: article
• Mynediad Ar-lein: Connect to this object online.

BackgroundAs a new non-factor therapy for hemophilia A (HA), real-world study of emicizumab is still scarce. This study aimed to investigate the real-world use of emicizumab in Chinese boys with HA.MethodsPatients with moderate or severe HA were enrolled at Beijing Children's Hospital. They tak...