New drugs in cystic fibrosis: what has changed in the last decade?

• Main Authors: Juliana Roda (Author), Catarina Pinto-Silva (Author), Iris A.I. Silva (Author), Carla Maia (Author), Susana Almeida (Author), Ricardo Ferreira (Author), Guiomar Oliveira (Author)
• Format: Book
• Published: SAGE Publishing, 2022-05-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Cystic fibrosis (CF), a life-limiting chronic disease caused by mutations in the cystic fibrosis transmembrane regulator (CFTR) gene, affects more than 90,000 people worldwide. Until recently, the only available treatments were directed to symptom control, but they failed to change the course of the...