Navigating the unknown: how to best 'reflect' standard of care in indications without a dedicated treatment pathway in health technology assessment submissions

• Huvudupphovsmän: Grammati Sarri (Författare, medförfattare), Maria Rizzo (Författare, medförfattare), Sheela Upadhyaya (Författare, medförfattare), Victoria Federico Paly (Författare, medförfattare), Luis Hernandez (Författare, medförfattare)
• Materialtyp: Bok
• Publicerad: Becaris Publishing Limited, 2024-01-01T00:00:00Z.
• Ämnen: article
• Länkar: Connect to this object online.

There is an urgent need for expedited approval and access for new health technologies targeting rare and very rare diseases, some of which are associated with high unmet treatment needs. Once a new technology achieves regulatory approval, the technology needs to be assessed by health technology asse...