Recent Trends in Antisense Therapies for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a debilitating and fatal genetic disease affecting 1/5000 boys globally, characterized by progressive muscle breakdown and eventual death, with an average lifespan in the mid-late twenties. While no cure yet exists for DMD, gene and antisense therapies have been...
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Main Authors: | Harry Wilton-Clark (Author), Toshifumi Yokota (Author) |
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Format: | Book |
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MDPI AG,
2023-02-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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