Treatment effectiveness in a rare oncology indication: Lessons from an external control cohort study

• Main Authors: Dina Oksen (Author), Patricia Prince (Author), Emmanuelle Boutmy (Author), Elizabeth M. Garry (Author), Barbara Ellers‐Lenz (Author), Adina Estrin (Author), Andreas Johne (Author), Patrice Verpillat (Author), Nicolle M. Gatto (Author)
• Format: Book
• Published: Wiley, 2022-08-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Abstract Real‐world data (RWD) reflecting patient treatment in routine clinical practice can be used to develop external control groups for single‐arm trials. External controls can provide valuable benchmark results on potential comparator drug effectiveness, particularly in rare indications when ra...