Mutation-Directed Therapeutics for Neurofibromatosis Type I

• Main Authors: Andre Leier (Author), David M. Bedwell (Author), Ann T. Chen (Author), George Dickson (Author), Kim M. Keeling (Author), Robert A. Kesterson (Author), Bruce R. Korf (Author), Tatiana T. Marquez Lago (Author), Ulrich F. Müller (Author), Linda Popplewell (Author), Jiangbing Zhou (Author), Deeann Wallis (Author)
• Format: Book
• Published: Elsevier, 2020-06-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Significant advances in biotechnology have led to the development of a number of different mutation-directed therapies. Some of these techniques have matured to a level that has allowed testing in clinical trials, but few have made it to approval by drug-regulatory bodies for the treatment of specif...