Alpha-1-Antitrypsin Deficiency in Children-Unmet Needs Concerning the Liver Manifestation

• Main Authors: Joelle Lemke (Author), Alexander Weigert (Author), Soyhan Bagci (Author), Mark Born (Author), Rainer Ganschow (Author), David Katzer (Author)
• Format: Book
• Published: MDPI AG, 2024-06-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Objectives: This study aimed to analyse the clinical course of 45 children with severe alpha-1-antitrypsin deficiency (AATD) registered in our clinic to detect possible predictors of poor outcomes. Methods: The clinical and biological data of 45 patients with homozygous or compound heterozygous AATD...