CASE SERIES OF PATIENTS UNDER BIWEEKLY TREATMENT WITH LARONIDASE: A REPORT OF A SINGLE CENTER EXPERIENCE

ABSTRACT Objective: To report the stabilization of urinary glycosaminoglicans (GAG) excretion and clinical improvements in patients with mucopolysaccharidosis type I (MPS I) under an alternative dose regimen of laronidase of 1.2 mg/kg every other week. Methods: We participated in a dose-optimization...

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Main Authors: Sandra Obikawa Kyosen (Author), Leny Toma (Author), Helena Bonciani Nader (Author), Marion Coting Braga (Author), Vanessa Gonçalves Pereira (Author), Sueli Canossa (Author), João Bosco Pesquero (Author), Vânia D'Almeida (Author), Ana Maria Martins (Author)
Format: Book
Published: Sociedade de Pediatria de São Paulo, 2019-05-01T00:00:00Z.
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3rd Floor Main Library

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Call Number: A1234.567
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