Assessment of the feasibility of exon 45-55 multiexon skipping for duchenne muscular dystrophy

• Главные авторы: van Ommen Gert-Jan B (Автор), van Deutekom Judith CT (Автор), de Winter Christa L (Автор), van Vliet Laura (Автор), Aartsma-Rus Annemieke (Автор)
• Формат: ‌
• Опубликовано: BMC, 2008-12-01T00:00:00Z.
• Предметы: article
• Online-ссылка: Connect to this object online.

<p>Abstract</p> <p>Background</p> <p>The specific skipping of an exon, induced by antisense oligonucleotides (AON) during splicing, has shown to be a promising therapeutic approach for Duchenne muscular dystrophy (DMD) patients. As different mutations require skipping o...