Safety and efficacy of trofinetide in Rett syndrome: a systematic review and meta-analysis of randomized controlled trials

• Autors principals: Abdallah Abbas (Autor), Aya M Fayoud (Autor), Mostafa Hossam El Din Moawad (Autor), Abdullah Ashraf Hamad (Autor), Heba Hamouda (Autor), Eman A. Fouad (Autor)
• Format: Llibre
• Publicat: BMC, 2024-03-01T00:00:00Z.
• Matèries: article
• Accés en línia: Connect to this object online.

Abstract Introduction Rett syndrome is a rare genetic neurodevelopmental disorder that predominantly impacts females. It presents with loss of acquired skills, impaired communication, and stereotypic hand movements. Given the limited treatment options for Rett syndrome, there is a dire need for effe...