Enzyme replacement therapy: efficacy and limitations

Abstract Enzyme replacement therapy (ERT) is available for mucopolysaccharidosis (MPS) I, MPS II, MPS VI, and MPS IVA. The efficacy of ERT has been evaluated in clinical trials and in many post-marketing studies with a long-term follow-up for MPS I, MPS II, and MPS VI. While ERT is effective in redu...

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Main Authors: Daniela Concolino (Author), Federica Deodato (Author), Rossella Parini (Author)
Format: Book
Published: BMC, 2018-11-01T00:00:00Z.
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3rd Floor Main Library

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Call Number: A1234.567
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