Positive Response to One-Year Treatment With Burosumab in Pediatric Patients With X-Linked Hypophosphatemia

• Main Authors: Silvia Martín Ramos (Author), Marta Gil-Calvo (Author), Virginia Roldán (Author), Ana Castellano Martínez (Author), Fernando Santos (Author)
• Formato: Livro
• Publicado em: Frontiers Media S.A., 2020-02-01T00:00:00Z.
• Assuntos: article
• Acesso em linha: Connect to this object online.

X-linked hypophosphatemia (XLH) causes significant burden in pediatric patients in spite of maintained treatment with phosphate supplements and vitamin D derivatives. Administration of burosumab has shown promising results in clinical trial but studies assessing its effect in the everyday practice a...