Estimating health state utilities in Duchenne muscular dystrophy using the health utilities index and EQ-5D-5L

• Main Authors: Ivana F. Audhya (Author), Shelagh M. Szabo (Author), Andrea Bever (Author), Fiona O'Sullivan (Author), Daniel C. Malone (Author), David Feeny (Author), Peter Neumann (Author), Susan T. Iannaccone (Author), P. Jayasinghe (Author), Katherine L. Gooch (Author)
• Format: Book
• Published: SpringerOpen, 2023-12-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Abstract Background The progression of Duchenne muscular dystrophy (DMD) is characterized by loss of ambulation, respiratory insufficiency, cardiomyopathy, and early mortality. DMD profoundly impacts health-related quality-of-life (HRQoL). However, few health state utility data exist; published util...