Utility estimations of different health states of patients with type I, II, and III spinal muscular atrophy in China: A mixed approach study with patient and proxy-reported data

• Main Authors: Jiahao Hu (Author), Lin Zhu (Author), Han Bao (Author), Yuhan Liu (Author), Huanping Xing (Author), Qi Kang (Author), Chunlin Jin (Author)
• Formato: Livro
• Publicado em: Frontiers Media S.A., 2022-12-01T00:00:00Z.
• Assuntos: article
• Acesso em linha: Connect to this object online.

IntroductionSpinal muscular atrophy (SMA) is a rare autosomal-recessive neuromuscular disease. Health state utility values (HSUV) are used in health economic evaluation regarding the desirability of health outcomes such as a certain health state or change in health states over time. There is no util...