Managing the challenges of paying for gene therapy: strategies for market action and policy reform in the United States

• Huvudskapare: Sharon Phares (Författare, medförfattare), Mark Trusheim (Författare, medförfattare), Sarah K Emond (Författare, medförfattare), Steven D Pearson (Författare, medförfattare)
• Materialtyp: Bok
• Publicerad: Becaris Publishing Limited, 2024-11-01T00:00:00Z.
• Ämnen: article
• Länkar: Connect to this object online.

Gene therapies delivered through a single administration have revolutionized treatment possibilities for many patients living with serious or fatal conditions such as spinal muscular atrophy, hemophilia and sickle cell disease. However, shadowing the excitement about the transformational potential o...