Managing the challenges of paying for gene therapy: strategies for market action and policy reform in the United States

• Main Authors: Sharon Phares (Author), Mark Trusheim (Author), Sarah K Emond (Author), Steven D Pearson (Author)
• Formato: Livro
• Publicado em: Becaris Publishing Limited, 2024-11-01T00:00:00Z.
• Assuntos: article
• Acesso em linha: Connect to this object online.

Gene therapies delivered through a single administration have revolutionized treatment possibilities for many patients living with serious or fatal conditions such as spinal muscular atrophy, hemophilia and sickle cell disease. However, shadowing the excitement about the transformational potential o...