Development of a novel PRO instrument for use in familial chylomicronemia syndrome

• Главные авторы: David Davidson (Автор), Christina Slota (Автор), Montserrat Vera-Llonch (Автор), T. Michelle Brown (Автор), Andrew Hsieh (Автор), Sheri Fehnel (Автор)
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• Опубликовано: SpringerOpen, 2021-08-01T00:00:00Z.
• Предметы: article
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Abstract Background Familial chylomicronemia syndrome (FCS), a rare genetic disorder characterized by high levels of circulating triglycerides, negatively impacts multiple organs, including the liver and pancreas. Objective The objective of this study was to develop and support the content validity...