Potential Disease-Modifying Effects of Lithium Carbonate in Niemann-Pick Disease, Type C1

• Main Authors: Shiqian Han (Author), Huiwen Zhang (Author), Mengni Yi (Author), Xiaoqing Liu (Author), Gustavo H. B. Maegawa (Author), Yunding Zou (Author), Qijun Wang (Author), Dianqing Wu (Author), Zhijia Ye (Author)
• Format: Book
• Published: Frontiers Media S.A., 2021-06-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Background: Niemann-Pick disease type C1 (NP-C1) is a rare, autosomal-recessive neurodegenerative disorder with no United States Food and Drug Administration (FDA)-approved drug. Lithium has been shown to have considerable neuroprotective effects for neurological disorders such as bipolar disorder,...