Hydrogel Delivery Device for the In Vitro and In Vivo Sustained Release of Active rhGALNS Enzyme

Morquio A disease is a genetic disorder resulting in N-acetylgalactosamine-6-sulfate sulfatase (GALNS) deficiency, and patients are currently treated with enzyme replacement therapy via weekly intravenous enzyme infusions. A means of sustained enzyme delivery could improve patient quality of life by...

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Váldodahkkit: Michael Flanagan (Dahkki), Qi Gan (Dahkki), Saahil Sheth (Dahkki), Rachel Schafer (Dahkki), Samuel Ruesing (Dahkki), Linda E. Winter (Dahkki), Karoly Toth (Dahkki), Silviya P. Zustiak (Dahkki), Adriana M. Montaño (Dahkki)
Materiálatiipa: Girji
Almmustuhtton: MDPI AG, 2023-06-01T00:00:00Z.
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3rd Floor Main Library

oažžasuvvan: 3rd Floor Main Library
Hildobáiki: A1234.567
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