Economic outcomes of centralized procurements of gene therapy for patients with orphan diseases: inherited retinal dystrophy

• Κύριοι συγγραφείς: N. А. Avxentyev (Συγγραφέας), Yu. V. Makarova (Συγγραφέας), V. V. Kadyshev (Συγγραφέας)
• Μορφή: Βιβλίο
• Έκδοση: IRBIS LLC, 2022-01-01T00:00:00Z.
• Θέματα: article
• Διαθέσιμο Online: Connect to this object online.

Background. New pathogenetic treatment options, such as gene therapy, are now used to treat previously uncurable diseases. However, price of such treatment is high, especially in the case of orphan diseases, where costs may many-fold exceed the prices for other types of medication. This raises a que...