Improving access to gene therapies: a holistic view of current challenges and future policy solutions in the United States

• Главные авторы: Tyler D Wagner (Автор), Lisabeth Buelt (Автор), Kimberly Westrich (Автор), Jonathan D Campbell (Автор)
• Формат: ‌
• Опубликовано: Becaris Publishing Limited, 2024-11-01T00:00:00Z.
• Предметы: article
• Online-ссылка: Connect to this object online.

Gene therapies hold the promise of delivering groundbreaking improvements in health outcomes for previously intractable diseases. These therapies possess unique characteristics that differ from traditional small molecule or biologic treatments, posing new challenges for healthcare stakeholders. Whil...