Research advances in treatment methods and drug development for rare diseases

• Main Authors: Qiaoqiao Han (Author), Hengtao Fu (Author), Xiaoyue Chu (Author), Ruixin Wen (Author), Miao Zhang (Author), Tao You (Author), Peng Fu (Author), Jian Qin (Author), Tao Cui (Author)
• Format: Book
• Published: Frontiers Media S.A., 2022-10-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

As the incidence of rare diseases increases each year, the total number of rare disease patients worldwide is nearly 400 million. Orphan medications are drugs used to treat rare diseases. Orphan drugs, however, are rare and patients often struggle to utilize them and expensive medications during tre...