An overview of health technology assessments of gene therapies with the focus on cost-effectiveness models

• Main Authors: Michał Pochopień (Author), Ewelina Paterak (Author), Emilie Clay (Author), Justyna Janik (Author), Samuel Aballea (Author), Małgorzata Biernikiewicz (Author), Mondher Toumi (Author)
• Format: Book
• Published: Taylor & Francis Group, 2021-01-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Background: Gene therapies can treat, prevent, or cure a disease by changing the expression of a person's genes. They are an innovative strategy for treating genetic disorders; however, they are still emerging on the market access and in the healthcare system. Health technology assessment (HTA)...