Clinical and Electrophysiological Changes in Pediatric Spinal Muscular Atrophy after 2 Years of Nusinersen Treatment

In the new therapeutic era, disease-modifying treatment (nusinersen) has changed the natural evolution of spinal muscular atrophy (SMA), creating new phenotypes. The main purpose of the retrospective observational study was to explore changes in clinical evolution and electrophysiological data after...

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Main Authors: Mihaela Axente (Author), Andrada Mirea (Author), Corina Sporea (Author), Liliana Pădure (Author), Cristina Manuela Drăgoi (Author), Alina Crenguța Nicolae (Author), Daniela Adriana Ion (Author)
Format: Book
Published: MDPI AG, 2022-09-01T00:00:00Z.
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3rd Floor Main Library

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Call Number: A1234.567
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