Homology-Directed-Repair-Based Genome Editing in HSPCs for the Treatment of Inborn Errors of Immunity and Blood Disorders
Genome engineering via targeted nucleases, specifically CRISPR-Cas9, has revolutionized the field of gene therapy research, providing a potential treatment for diseases of the blood and immune system. While numerous genome editing techniques have been used, CRISPR-Cas9 homology-directed repair (HDR)...
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| Main Authors: | , , , |
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| Format: | Book |
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MDPI AG,
2023-04-01T00:00:00Z.
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| Call Number: |
A1234.567 |
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| Copy 1 | Available |