Microbubble drug conjugate and focused ultrasound blood brain barrier delivery of AAV-2 SIRT-3

Background Delivery of viral vectors as gene therapies to treat neurodegenerative diseases has been hampered by the inability to penetrate the blood brain barrier (BBB) and invasive or non-targeted delivery options prone to inducing immune responses. MR guided focused ultrasound (MR-g-FUS) and micro...

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Egile Nagusiak: Dennison Trinh (Egilea), Joanne Nash (Egilea), David Goertz (Egilea), Kullervo Hynynen (Egilea), Sharshi Bulner (Egilea), Umar Iqbal (Egilea), James Keenan (Egilea)
Formatua: Liburua
Argitaratua: Taylor & Francis Group, 2022-12-01T00:00:00Z.
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