Parents' dilemma: A therapeutic decision for children with spinal muscular atrophy (SMA) type 1

• প্রধান লেখক: Sophie Boursange (লেখক), Marco Araneda (লেখক), Caroline Stalens (লেখক), Isabelle Desguerre (লেখক), Christine Barnerias (লেখক), Marie-Christine Nougues (লেখক), Arnaud Isapof (লেখক), Susana Quijano-Roy (লেখক), Nadia Blu Genestine (লেখক), Laetitia Ouillade (লেখক), Maripaz Martinez Jalilie (লেখক), Claudia Castiglioni (লেখক), Odile Boespflug-Tanguy (লেখক), Marcela Gargiulo (লেখক), The SMAPAR Study Group (লেখক)
• বিন্যাস: গ্রন্থ
• প্রকাশিত: Frontiers Media S.A., 2022-12-01T00:00:00Z.
• বিষয়গুলি: article
• অনলাইন ব্যবহার করুন: Connect to this object online.

BackgroundSMA type 1 is a severe neurodegenerative disorder that, in the absence of curative treatment, leads to death before 1 year of age without ventilatory support. Three innovative therapies are available to increase life expectancy.Purpose(i) To increase knowledge about parents' experienc...