Gaucher disease in Brazil: a comprehensive 16 year retrospective study on survival, cost, and treatment insights

• Main Authors: Marcus Carvalho Borin (Author), Juliana Alvares-Teodoro (Author), Francisco Assis Acurcio (Author), Augusto Afonso Guerra (Author)
• Format: Book
• Published: Frontiers Media S.A., 2024-09-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

BackgroundGaucher's disease (GD), a lysosomal storage disorder, poses significant treatment challenges. This 23-year study assesses survival rates and treatment efficacy in Brazilian GD patients, integrating data from a 16-year cohort (2000-2015) and the TABNET/DATASUS medicines distribution da...