Psychometric performance of the Primary Mitochondrial Myopathy Symptom Assessment (PMMSA) in a randomized, double-blind, placebo-controlled crossover study in subjects with mitochondrial disease

• Main Authors: Chad Gwaltney (Author), Jonathan Stokes (Author), Anthony Aiudi (Author), Iyar Mazar (Author), Sarah Ollis (Author), Emily Love (Author), Amel Karaa (Author), Carrie R. Houts (Author), R. J. Wirth (Author), Alan L. Shields (Author)
• Format: Book
• Published: SpringerOpen, 2022-12-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Abstract Background The Primary Mitochondrial Myopathy Symptom Assessment (PMMSA) is a 10-item patient-reported outcome (PRO) measure designed to assess the severity of mitochondrial disease symptoms. Analyses of data from a clinical trial with PMM patients were conducted to evaluate the psychometri...