Nusinersen Administration in Spinal Muscular Atrophy Patients with Severe Scoliosis: Interlaminar Approaches at the Lumbar Level

• Hauptverfasser: Joo Young Song (Verfasst von), Hyun Su Kim (Verfasst von), Se-Jun Park (Verfasst von), Jiwon Lee (Verfasst von), Jeehun Lee (Verfasst von)
• Format: Buch
• Veröffentlicht: Korean Child Neurology Society, 2020-04-01T00:00:00Z.
• Schlagworte: article
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Purpose Spinal muscular atrophy (SMA) is a genetic progressive neuromuscular disorder, and nusinersen has shown to improve its symptoms. Scoliosis is a frequent symptom in patients with SMA and complicates the intrathecal injection of nusinersen. The aim of this study was to investigate the safety a...