Efficacy and safety of thalidomide in children with monogenic autoinflammatory diseases: a single-center, real-world-evidence study

• Egile Nagusiak: Caihui Zhang (Egilea), Zhongxun Yu (Egilea), Sihao Gao (Egilea), Mingsheng Ma (Egilea), Lijuan Gou (Egilea), Changyan Wang (Egilea), Lin Wang (Egilea), Ji Li (Egilea), Linqing Zhong (Egilea), Yu Zhou (Egilea), Wei Wang (Egilea), Hongmei Song (Egilea)
• Formatua: Liburua
• Argitaratua: BMC, 2023-10-01T00:00:00Z.
• Gaiak: article
• Sarrera elektronikoa: Connect to this object online.

Abstract Background Monogenic autoinflammatory diseases (AIDs) are rare inflammatory diseases caused by genetic variants. The pathogenesis is complex and treatment options are limited. This study aimed to describe the safety and efficacy of thalidomide in the treatment of monogenic AIDs. Methods Thi...