Theragnosis for Duchenne Muscular Dystrophy

• Main Authors: Leonela Luce (Author), Micaela Carcione (Author), Chiara Mazzanti (Author), Paula I. Buonfiglio (Author), Viviana Dalamón (Author), Lilia Mesa (Author), Alberto Dubrovsky (Author), José Corderí (Author), Florencia Giliberto (Author)
• Format: Book
• Published: Frontiers Media S.A., 2021-06-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Dystrophinopathies cover a spectrum of rare progressive X-linked muscle diseases, arising from DMD mutations. They are among the most common pediatric muscular dystrophies, being Duchenne muscular dystrophy (DMD) the most severe form. Despite the fact that there is still no cure for these serious di...