Hematopoietic Stem Cell Transplantation in Inborn Errors of Metabolism
Hematopoietic stem cell transplantation (HSCT) has been established as an effective therapy for selected inborn errors of metabolism. The success of HSCT in metabolic disease is best exemplified through the treatment of Hurler's syndrome, a lysosomal storage disease. Through the collaborative e...
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Формат: | Книга |
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Frontiers Media S.A.,
2019-10-01T00:00:00Z.
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Connect to this object online.3rd Floor Main Library
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A1234.567 |
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