Inotersen: new promise for the treatment of hereditary transthyretin amyloidosis

Veena Mathew,1 Annabel K Wang1,2 1Department of Neurology, UCI ALS and Neuromuscular Center, University of California, Irvine, Orange, CA, USA; 2Neurology Section, Tibor Rubin VA Medical Center, Long Beach, CA, USA Abstract: Hereditary transthyretin amyloidosis is a fatal autosomal dominant disorder...

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Egile Nagusiak: Mathew V (Egilea), Wang AK (Egilea)
Formatua: Liburua
Argitaratua: Dove Medical Press, 2019-05-01T00:00:00Z.
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