Histone deacetylase inhibitors improve antisense-mediated exon-skipping efficacy in mdx mice

Antisense-mediated exon skipping is one of the most promising therapeutic strategies for Duchenne muscular dystrophy (DMD), and some antisense oligonucleotide (ASO) drugs have already been approved by the US FDA despite their low efficacy. The potential of this therapy is still limited by several ch...

Full description

Saved in:
Bibliographic Details
Main Authors: Flavien Bizot (Author), Remko Goossens (Author), Thomas Tensorer (Author), Sergei Dmitriev (Author), Luis Garcia (Author), Annemieke Aartsma-Rus (Author), Pietro Spitali (Author), Aurélie Goyenvalle (Author)
Format: Book
Published: Elsevier, 2022-12-01T00:00:00Z.
Subjects:
Online Access:Connect to this object online.
Tags: Add Tag
No Tags, Be the first to tag this record!

Internet

Connect to this object online.

3rd Floor Main Library

Holdings details from 3rd Floor Main Library
Call Number: A1234.567
Copy 1 Available