Drug development progress in duchenne muscular dystrophy

• Auteurs principaux: Jiexin Deng (Auteur), Junshi Zhang (Auteur), Keli Shi (Auteur), Zhigang Liu (Auteur)
• Format: Livre
• Publié: Frontiers Media S.A., 2022-07-01T00:00:00Z.
• Sujets: article
• Accès en ligne: Connect to this object online.

Duchenne muscular dystrophy (DMD) is a severe, progressive, and incurable X-linked disorder caused by mutations in the dystrophin gene. Patients with DMD have an absence of functional dystrophin protein, which results in chronic damage of muscle fibers during contraction, thus leading to deteriorati...