Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA

• Main Authors: Joel Iff (Author), Yi Zhon (Author), Edward Tuttle (Author), Deepshekhar Gupta (Author), Xander Paul (Author), Erik Henricson (Author)
• Format: Book
• Published: Becaris Publishing Limited, 2023-08-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Aim: To evaluate treatment effects of eteplirsen among patients with Duchenne muscular dystrophy. Methods: Using real-world claims and electronic medical record data, this retrospective comparative analysis assessed eteplirsen-treated and control cohorts matched by age, disease progression state, an...