EXPERIENCE OF IMPLEMENTING NEW TECHNOLOGY TREATMENT OF CHILDREN WITH MPS IN THE RUSSIAN PEDIATRIC PRACTICE

The paper is devoted to one of the rare genetically determined diseases - mucopolysaccharidosis. Despite the great achievement of science - the development of the pathogenetic enzyme replacement therapy, many challenges remain. Among them - the lack of timely diagnosis, causing delayed treatment and...

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Päätekijät: A.A. Baranov (Tekijä), L.S. Namazova-Baranova (Tekijä), A.K. Gevorkyan (Tekijä), V.M. Krasnov (Tekijä), L.M. Kuzenkova (Tekijä), G.A. Kashkaradze (Tekijä), N.D. Vashakmadze (Tekijä), T.V. Podkletnova (Tekijä)
Aineistotyyppi: Kirja
Julkaistu: Union of pediatricians of Russia, 2011-10-01T00:00:00Z.
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