Adherence to Cysteamine Therapy Among Patients Diagnosed with Cystinosis in Saudi Arabia: A Prospective Cohort Study

• Hoofdauteurs: Reem Algasem (Auteur), Nedaa Zainy (Auteur), Essam Alsabban (Auteur), Hamad Almojalli (Auteur), Khalid Alhasan (Auteur), Tariq Ali (Auteur), Deiter Broering (Auteur), Hassan Aleid (Auteur)
• Formaat: Boek
• Gepubliceerd in: MDPI AG, 2024-08-01T00:00:00Z.
• Onderwerpen: article
• Online toegang: Connect to this object online.

Cystinosis is a rare autosomal recessive disorder in which cystine crystals accumulate within the cellular lysosomes, causing damage to multiple organs. Due to challenges with the stringent cysteamine treatment regimen and side effects, adherence is often sub-optimal. This study aimed to assess the...