Evaluation of the Efficacy of Nusinersen Treatment in Patients with Late-onset SMA Using the Hammersmith Functional Motor Scale Expanded

• Main Authors: Yiğithan Güzin (Author), Ayşe Özbay Yıldız (Author), Bakiye Tunçay (Author), Pınar Gençpınar (Author), Figen Baydan (Author), Nihal Olgaç Dündar (Author)
• Format: Book
• Published: Galenos Publishing House, 2024-08-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Objective: Spinal muscular atrophy (SMA) is a hereditary disorder with progressive muscle weakness and atrophy. Nusinersen is an antisense oligonucleotide directed against SMN2 and has been shown in studies to improve the motor skills of patients. The aim of this study was to evaluate the efficacy o...