Emicizumab in children: bleeding episodes and outcome before and after transition to Emicizumab

• Main Authors: Hannah Glonnegger (Author), Felicia Andresen (Author), Friedrich Kapp (Author), Stefano Malvestiti (Author), Martin Büchsel (Author), Barbara Zieger (Author)
• Format: Book
• Published: BMC, 2022-08-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Abstract Purpose Real-world data and study data regarding therapy with Emicizumab in pediatric cohorts with haemophilia A is scarce. Especially, data on previously untreated pediatric patients (PUPs) and minimally treated patients (MTPs) are missing. Methods Thirteen pediatric patients with haemophi...