THE IMPACT OF EVINACUMAB THERAPY ON PEDIATRIC PATIENTS WITH HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA: RESULTS FROM PART B OF A PHASE 3 TRIAL

• Main Authors: Albert Wiegman (Author), Susanne Greber-Platzer (Author), Shazia Ali (Author), Divya Singh (Author), M. Doortje Reijman (Author), Eliot A Brinton (Author), Min-Ji Charng (Author), Shubha Srinivasan (Author), Carissa Baker-Smith (Author), Seth Baum (Author), Julie Brothers (Author), Jacob Hartz (Author), Patrick M. Moriarty (Author), Poulabi Banerjee (Author), Richard T George (Author), Robert Pordy (Author)
• Formato: Livro
• Publicado em: Elsevier, 2023-09-01T00:00:00Z.
• Assuntos: article
• Acesso em linha: Connect to this object online.

Therapeutic Area: ASCVD /CVD Risk Reduction Background: Homozygous familial hypercholesterolemia (HoFH) is a rare genetic disorder characterized by severely elevated low-density lipoprotein cholesterol (LDL-C) levels. Currently, few treatments effectively lower LDL-C levels in pediatric patients wit...