New therapeutic modalities for rare diseases

• Huvudskapare: Fatih S. Ezgu (Författare, medförfattare)
• Materialtyp: Bok
• Publicerad: Elsevier, 2024-03-01T00:00:00Z.
• Ämnen: article
• Länkar: Connect to this object online.

Genetic Diseases affect about 2 % to 3 % of all live births. It has been reported that genetic disorders can account for up to 22 % of infant deaths. Despite this significant effort to create new therapies, treatment is available only for about 5 % of these diseases due to undiscovered etiology or r...