The cost-effectiveness of pegcetacoplan in complement treatment-naive adults with paroxysmal nocturnal hemoglobinuria in the USA

• मुख्य लेखकों: Jesse Fishman (लेखक), Koo Wilson (लेखक), Aleksandra Drzewiecka (लेखक), Michal Pochopien (लेखक), David Dingli (लेखक)
• स्वरूप: पुस्तक
• प्रकाशित: Becaris Publishing Limited, 2023-09-01T00:00:00Z.
• विषय: article
• ऑनलाइन पहुंच: Connect to this object online.

Aim: Paroxysmal nocturnal hemoglobinuria (PNH) is a rare blood disorder characterized by hemolytic anemia, bone marrow failure and thrombosis, and is associated with high healthcare burden. We evaluated the cost-effectiveness of pegcetacoplan, a proximal complement-3 inhibitor (C3i), compared with t...