Economic evaluation of betibeglogene autotemcel (Beti-cel) gene addition therapy in transfusion-dependent β-thalassemia

• Main Authors: Anuraag R. Kansal (Author), Odette S. Reifsnider (Author), Sarah B. Brand (Author), Neil Hawkins (Author), Anna Coughlan (Author), Shujun Li (Author), Lael Cragin (Author), Clark Paramore (Author), Andrew C. Dietz (Author), J. Jaime Caro (Author)
• Format: Book
• Published: Taylor & Francis Group, 2021-01-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Background Standard of care (SoC) for transfusion-dependent β-thalassemia (TDT) requires lifelong, regular blood transfusions as well as chelation to reduce iron accumulation. Objective This study investigates the cost-effectiveness of betibeglogene autotemcel ('beti-cel'; LentiGlobin for...