Psychometric evaluation of a patient-reported outcomes instrument for congenital thrombotic thrombocytopenic purpura

• Үндсэн зохиолчид: Abiola Oladapo (Зохиогч), Diane Ito (Зохиогч), Ana María Rodriguez (Зохиогч), Stephanie Philpott (Зохиогч), Robert Krupnick (Зохиогч), Veleka Allen (Зохиогч), Christopher Hibbard (Зохиогч), Marie Scully (Зохиогч), Bruce Ewenstein (Зохиогч)
• Формат: Ном
• Хэвлэсэн: SpringerOpen, 2023-07-01T00:00:00Z.
• Нөхцлүүд: article
• Онлайн хандалт: Connect to this object online.

Abstract Background Congenital thrombotic thrombocytopenic purpura (cTTP) is an ultra-rare, life-threatening hereditary disorder that causes patients to experience significant morbidity and decreased health-related quality of life (HRQoL). A cTTP disease-specific patient-reported outcome (PRO) instr...